Clinical Trials
These are research done initially in a very small number of patients, and subsequently larger numbers before any therapy into diseases is approved by the regulatory authorities of the country. www.clinicaltrials.gov gives a comprehensive list of clinical trials being conducted around the world in Inherited Retinal Diseases. Foundation Fighting Blindness (www.fightblindness.org) is driving research into […]
Clinical Trials
These are research done initially in a very small number of patients, and subsequently larger numbers before any therapy into diseases is approved by the regulatory authorities of the country. www.clinicaltrials.gov gives a comprehensive list of clinical trials being conducted around the world in Inherited Retinal Diseases. Foundation Fighting Blindness (www.fightblindness.org) is driving research into […]
Gene Therapy
Gene therapy involves replacing the defective gene with a correct one that is encapsulated within a viral capsid. Once injected, the virus replicates allowing for delivery of the corrected gene. Given that the pathway is different for each genetic mutation, gene therapy is an expensive treatment. Several clinical trials are underway to treat various […]